NEWSWORTHY
Boy with rare disease playing again with new gene-edited skin
A boy who nearly died when disease stripped most of the skin from his body, is playing soccer two years after he received a new, gene-edited hide in an experimental procedure, the doctors who treated him said Wednesday. The boy, then 7 years old, was ...
Gene therapy has dramatically improved the conditions of two bedridden teens suffering from a rare disease, Jichi Medical University said Tuesday. The Tochigi Prefecture-based university said that the finding could lead to the development of treatment for other rare neurological diseases. The two teens have a ...
Gene therapy for deafness is moving closer to reality, with new research on Wednesday showing the technique for fixing faulty DNA can improve responses in mice with genetic hearing loss. Separately, a clinical trial backed by Novartis is under way to help a different group ...
Gene therapy seen offering promise to some cystic fibrosis patients
Doctors who gave children with cystic fibrosis a replacement copy of a defective gene say it appeared to slow the expected decline of some patients' lungs, but called the results "modest" and say there must be major improvements before offering the treatment more widely. Cystic ...
