Doctors use HIV in gene therapy to fix babies' 'bubble boy' disease
They were born without a working germ-fighting system, every infection a threat to their lives. Now eight babies with "bubble boy disease" have had it fixed by a gene therapy made from one of the immune system's worst enemies — HIV, the virus that ...
Gene therapy has dramatically improved the conditions of two bedridden teens suffering from a rare disease, Jichi Medical University said Tuesday. The Tochigi Prefecture-based university said that the finding could lead to the development of treatment for other rare neurological diseases. The two teens have a ...
Gene therapy for deafness is moving closer to reality, with new research on Wednesday showing the technique for fixing faulty DNA can improve responses in mice with genetic hearing loss. Separately, a clinical trial backed by Novartis is under way to help a different group ...
Gene therapy seen offering promise to some cystic fibrosis patients
Doctors who gave children with cystic fibrosis a replacement copy of a defective gene say it appeared to slow the expected decline of some patients' lungs, but called the results "modest" and say there must be major improvements before offering the treatment more widely. Cystic ...
